The process of developing a treatment must go through these steps:

1. Therapeutic Design and AI/ML optimization
2. Pharmacology and Non-GLP Toxicology
3. Type B PreIND FDA Meeting
4. Manufacturing Scale-up and Controls
5. GLP toxicology
6. GMP Production
7. IND submission
8. Phase I/II clinical trial

The cost of it is estimated to $8 000 000. We need your help to allow researchers from Genethon and CRD go through this beautiful project.

Every donation counts!

Please contact us and we’ll be glad to tell the best way to help our community.